A Study to Evaluate the Effectiveness and Safety of Prephase Steroid Treatment before Remission Induction Chemotherapy in Patients with Pediatric Acute Lymphoblastic Leukemia Using Common Data Model-Based Real-World Data: A Retrospective Observational Study

References

• Cooper SL, Brown PA. Treatment of pediatric acute lymphoblastic leukemia. Pediatr Clin North Am. 2015;62(1):61–73. doi:10.1016/j.pcl.2014.09.006
   PubMed Web of Science ®Google Scholar
• Bassan R, Hoelzer D. Modern therapy of acute lymphoblastic leukemia. J Clin Oncol. 2011;29(5):532–543. doi:10.1200/JCO.2010.30.1382
   PubMed Web of Science ®Google Scholar
• Inaba H, Greaves M, Mullighan C. Acute lymphoblastic leukaemia. Lancet. 2013;381(9881):1943–1955. doi:10.1016/S0140-6736(12)62187-4
   PubMed Web of Science ®Google Scholar
• Seibel N. Treatment of acute lymphoblastic leukemia in children and adolescents: peaks and pitfalls. Hematology Am Soc Hematol Educ Program. 2008;2008(1):374–380. doi:10.1182/asheducation-2008.1.374
   Google Scholar
• Wilson FP, Berns JS. Tumor Lysis Syndrome: New Challenges and Recent Advances. Adv Chronic Kidney Dis. 2014;21(1):18–26. doi:10.1053/j.ackd.2013.07.001
   PubMed Web of Science ®Google Scholar
• Schrappe M, Reiter A, Zimmermann M, et al. Long-term results of four consecutive trials in childhood ALL performed by the ALL-BFM study group from 1981 to 1995. Berlin-Frankfurt-Munster Leukemia. 2000;14:2205–2222.
   PubMed Web of Science ®Google Scholar
• Reiter A, Schrappe M, Ludwig WD, et al. Chemotherapy in 998 unselected childhood acute lymphoblastic leukemia patients. Results and conclusions of the multicenter trial ALL-BFM 86. Blood. 1994;84(9):3122–3133. doi:10.1182/blood.V84.9.3122.3122
   PubMed Web of Science ®Google Scholar
• McNeer JL, Nachman JB. The optimal use of steroids in paediatric acute lymphoblastic leukaemia: no easy answers. Br J Haematol. 2010;149(5):638–652. doi:10.1111/j.1365-2141.2010.08192.x
   PubMed Web of Science ®Google Scholar
• Hunger SP, Lu X, Devidas M, et al. Improved Survival for Children and Adolescents With Acute Lymphoblastic Leukemia Between 1990 and 2005: A Report From the Children’s Oncology Group. J clin oncol. 2012;30(14):1663–1669. doi:10.1200/JCO.2011.37.8018
   PubMed Web of Science ®Google Scholar
• Dinnel J, Moore BL, Skiver BM, Bose P. Rasburicase in the management of tumor lysis: an evidence-based review of its place in therapy. Core Evid. 2015;10:23–38. doi:10.2147/CE.S54995
   PubMedGoogle Scholar
• Cairo MS, Bishop M. Tumour lysis syndrome: new therapeutic strategies and classification. Br J Haematol. 2004;127(1):3–11. doi:10.1111/j.1365-2141.2004.05094.x
   PubMed Web of Science ®Google Scholar
• American Diabetes A. Classification and Diagnosis of Diabetes: Standards of Medical Care in Diabetes-2020. Diabetes Care. 2020;43:S14–S31.
   PubMedGoogle Scholar
• Chesnaye NC, Stel VS, Tripepi G, et al. An introduction to inverse probability of treatment weighting in observational research. Clin Kidney J. 2021;15(1):14–20. doi:10.1093/ckj/sfab158
   PubMed Web of Science ®Google Scholar
• Austin PC. Balance diagnostics for comparing the distribution of baseline covariates between treatment groups in propensity-score matched samples. Stat Med. 2009;28(25):3083–3107. doi:10.1002/sim.3697
   PubMed Web of Science ®Google Scholar
• Ho D, Imai K, King G, Stuart EA. MatchIt: Nonparametric preprocessing for parametric causal inference. J Statistical Software. 2011;42(8):1–28. doi:10.18637/jss.v042.i08
   Web of Science ®Google Scholar
• Bursac Z, Gauss CH, Williams DK, Hosmer DW. Purposeful selection of variables in logistic regression. Source Code Biol Med. 2008;3(1):17. doi:10.1186/1751-0473-3-17
   PubMedGoogle Scholar
• Austin PC. An Introduction to Propensity Score Methods for Reducing the Effects of Confounding in Observational Studies. Multivariate Behav Res. 2011;46(3):399–424. doi:10.1080/00273171.2011.568786
   PubMed Web of Science ®Google Scholar
• Xue Y, Chen J, Gao S, et al. Clinical characteristics of tumor lysis syndrome in childhood acute lymphoblastic leukemia. Sci Rep. 2021;11(1):9656. doi:10.1038/s41598-021-88912-2
   PubMed Web of Science ®Google Scholar
• Schneeweiss S. Sensitivity analysis and external adjustment for unmeasured confounders in epidemiologic database studies of therapeutics. Pharmacoepidemiol Drug Saf. 2006;15(5):291–303. doi:10.1002/pds.1200
   PubMed Web of Science ®Google Scholar
• Lipsitch M, Tchetgen Tchetgen E, Cohen T. Negative controls: a tool for detecting confounding and bias in observational studies. Epidemiology. 2010;21(3):383–388. doi:10.1097/EDE.0b013e3181d61eeb
   PubMed Web of Science ®Google Scholar
• Swerdlow SH, Campo E, Harris NL, et al. WHO classification of tumours of haematopoietic and lymphoid tissues. International agency for research on cancer: Lyon, France; 2008.
   Google Scholar
• Onciu M. Acute lymphoblastic leukemia. Hematol Oncol Clin North Am. 2009;23(4):655–674. doi:10.1016/j.hoc.2009.04.009
   PubMed Web of Science ®Google Scholar
• Zhang J, Yu KF. What’s the relative risk? A method of correcting the odds ratio in cohort studies of common outcomes. JAMA. 1998;280(19):1690–1691. doi:10.1001/jama.280.19.1690
   PubMed Web of Science ®Google Scholar
• National Comprehensive Cancer Network. Pediatric Acute Lymphoblastic Leukemia (Version 2.2023); 2023.
   Google Scholar
• Jabbar N, Mansoor N, Nadeem K, Maqsood MS, Butt Z, Ashraf S. Prednisolone Prophase for a Week Versus Upfront Multiagent Chemotherapy in Childhood Acute Lymphoblastic Leukemia: An Analysis With Reference to Induction Mortality in a Developing Country. J Pediatr Hematol Oncol. 2020;42(3):181–184. doi:10.1097/MPH.0000000000001636
   PubMed Web of Science ®Google Scholar
• Grigorian A, O’Brien CB. Hepatotoxicity Secondary to Chemotherapy. J Clin Transl Hepatol. 2014;2(2):95–102. doi:10.14218/JCTH.2014.00011
   PubMedGoogle Scholar
• Liu D, Ahmet A, Ward L, et al. A practical guide to the monitoring and management of the complications of systemic corticosteroid therapy. Allergy Asthma Clin Immunol. 2013;9(1):30. doi:10.1186/1710-1492-9-30
   PubMed Web of Science ®Google Scholar
• Riehm H, Reiter A, Schrappe M, et al. Corticosteroid-dependent reduction of leukocyte count in blood as a prognostic factor in acute lymphoblastic leukemia in childhood (therapy study ALL-BFM 83). Klin Padiatrie. 1987;199(03):151–160. doi:10.1055/s-2008-1026781
   PubMedGoogle Scholar
• Schrappe M, Reiter A, Sauter S, et al. Concept and interim result of the ALL-BFM 90 therapy study in treatment of acute lymphoblastic leukemia in children and adolescents: the significance of initial therapy response in blood and bone marrow. Klin Padiatrie. 1994;206(04):208–221. doi:10.1055/s-2008-1046607
   PubMedGoogle Scholar
• Borowitz MJ, Devidas M, Hunger SP, et al. Clinical significance of minimal residual disease in childhood acute lymphoblastic leukemia and its relationship to other prognostic factors: a Children’s Oncology Group study. Blood. 2008;111(12):5477–5485. doi:10.1182/blood-2008-01-132837
   PubMed Web of Science ®Google Scholar
• Conter V, Bartram CR, Valsecchi MG, et al. Molecular response to treatment redefines all prognostic factors in children and adolescents with B-cell precursor acute lymphoblastic leukemia: results in 3184 patients of the AIEOP-BFM ALL 2000 study. Blood. 2010;115(16):3206–3214. doi:10.1182/blood-2009-10-248146
   PubMed Web of Science ®Google Scholar
• Cairo MS, Coiffier B, Reiter A, Younes A, Panel TLSE. Recommendations for the evaluation of risk and prophylaxis of tumour lysis syndrome (TLS) in adults and children with malignant diseases: an expert TLS panel consensus. Br J Haematol. 2010;149(4):578–586. doi:10.1111/j.1365-2141.2010.08143.x
   PubMed Web of Science ®Google Scholar
• OHDSI. The Book of OHDSI: Observational Health Data Sciences and Informatics. OHDSI; 2019.
   Google Scholar