Supplemental material
Open access
2,353
Views
2
CrossRef citations to date
0
Altmetric
Orphan Drugs
Value-based decision-making for orphan drugs with multiple criteria decision analysis: burosumab for the treatment of X-linked hypophosphatemia
Björn Vandewallea Exigo Consultores, Lisbon, PortugalCorrespondence[email protected]
, Miguel Amorima Exigo Consultores, Lisbon, Portugal
, Diogo Ramosa Exigo Consultores, Lisbon, Portugal
, Sofia Azevedoa Exigo Consultores, Lisbon, Portugal
, Inês Alvesb Associação Nacional de Displasias Ósseas, Évora, Portugal
, Telma Franciscoc Centro Hospitalar Universitário Lisboa Central, Lisbon, Portugal
, Helena Pintod Centro Hospitalar Universitário de São João, Porto, Portugal
& Sérgio Sousae Centro Hospitalar e Universitário de Coimbra, Coimbra, Portugal
show all
Pages 1021-1030
|
Received 26 Nov 2020, Accepted 14 Mar 2021, Published online: 01 Apr 2021
Related research
People also read lists articles that other readers of this article have read.
Recommended articles lists articles that we recommend and is powered by our AI driven recommendation engine.
Cited by lists all citing articles based on Crossref citations.
Articles with the Crossref icon will open in a new tab.