8,249
Views
6
CrossRef citations to date
0
Altmetric
Drug Evaluation

Risdiplam: an investigational survival motor neuron 2 (SMN2) splicing modifier for spinal muscular atrophy (SMA)

ORCID Icon, ORCID Icon, ORCID Icon & ORCID Icon
Pages 451-461 | Received 17 Dec 2021, Accepted 20 Mar 2022, Published online: 11 Apr 2022